Research Studies

If you are interested in participating in research, please contact:

Sarah Marler, MA, CPA
Program Coordinator


Autism Research


Stamped-FLYER 161917.jpgPediatric and Adolescent Medication Study – Autism

The aViation study will test a potential new treatment for ‘high-functioning’ autism spectrum disorder (ASD). The investigational study drug blocks a hormone receptor in the brain that is linked to the control of socialization, stress, anxiety and aggression. Participation lasts for up to 39 weeks. For 24 of those weeks, they will take daily doses of either the investigational study drug or a placebo (a look-alike) that contains no medicine. Both the investigational study drug and the placebo are small tablets that can be swallowed whole or dissolved in liquid. Participants and their parent or guardian will visit a study clinic around once every 6 weeks (about 7 times in total). This will allow the study team to assess their general health, social communication skills and social interaction skills. In between these clinic visits, a nurse will need to take some additional blood samples. To do this, they’ll either visit you at your home or you’ll be asked to go back to the clinic. Visits may include questionnaires, blood/urine samples, cognitive testing or physical exams at no cost to you. 



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Child Biomarker Study – Autism, Developmental Delay, and Typically Developing

We need children, between the ages of 18 months and 48 months. We are looking for typically developing children, as well as those with known/suspected Autism Spectrum Disorder/Developmental Delay. The study involves 1-3 visits over 2 years. Visits may include behavioral and cognitive assessments, blood or urine samples, or physical exams at no cost to you. Your time will be compensated.






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Pediatric Autism Study

We need children, between the ages of 3 and 8, with Autism to take part in a medication study at Vanderbilt. The study involves 9 visits over 12 weeks. Visits may include questionnaires, stool samples, or physical exams at no cost to you. CM-AT is developed by Curemark LLC, a drug research and development company focused on the treatment of neurological diseases. CM-AT is based on Curemark’s recent research that showed enzyme deficiencies in some autistic children result in an inability to digest protein. The inability to digest protein affects the production of amino acids, the building blocks of chemicals essential for brain function. 







Fragile X/Angelman Research

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Adolescent Medication Study

We need adolescents age 13– 17 for a study using of an investigational medication for Fragile X and Angelman syndromes. Evaluations, study visits, and study drug are 

provided at no cost. Compensation for your time will be provided. Travel may be reimbursed, depending on need. You will be asked to come for 2 visits to Vanderbilt University in Nashville, TN over 2 weeks to take part in this research study. A blood draw is required. Participant must be able to swallow a capsule. 





Down syndrome Research

No current trials in Down syndrome. Please keep checking back and sign up for our newsletter for more updates!